Custom Oligonucleotide Therapeutics Synthesis
Catalog Number: Oligonucleotide Therapeutics
Size(s): 2 mg – 5 mg, 5 mg – 20 mg, 20 mg -g-scale
High Purity
200+ Modifications
Minimal Impurities
100+ quality control methods
siRNA, miRNA, ASD,O, Aptamer, sgRNA and Stock Products
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You are enquiring about Custom Oligonucleotide Therapeutics Synthesis
Oligonucleotide Therapeutics Synthesis
Rapid, high-purity, and professional therapeutics synthesis.
With 15 years of expertise in oligonucleotide synthesis, our supplier leverages a well-established oligonucleotide chemistry platform and a robust quality control system to deliver high-purity oligonucleotides ranging from nmol to hundred-gram scale. We provide integrated, one-stop support to accelerate the development of small nucleic acids therapeutics.
Product Features
Fast
- 2 mg – 5 mg
- 5 mg – 20 mg
- 20 mg -g-scale
High Purity: Purifity: > 90%
200+ Modifications
- GalNAc, lipid, peptide, a nd small molecule conjugation
- Antibody conjugation (ADC)
- Dual-target oligonucleotide
Stabilizing modifications: 2’Ome, 2’-O-OmE, 2’F, 2’-O-C16, LNA, cEt, GNA, UNA
Chemical Modification: Biotin, Dual Biotin, Amino linker C6, Amino linker C7, Amino linker C12, Cholesterol, Digoxigenin
Bases Modification: Pseudouridine, 1-Methyl-PseudoUridine, m6A, m5C, rl
Spacers & Linkers: dSpacer, PC-Linker, Spacer 9, Spacer, 18, Spacer C3, Spacer C6, Spacer C12, Inverted Abasic
Phosphorylation: Phosphate, Phosphorothioate, 5’-(E)-VP
Targeting Ligand Conjugation: GalNAc L96, NAG37, NAG25, 2’O-C16, avB6
Minimal Impurities
- Patented RNA synthesis technology
- Single impurity < 1%
Quality Control
We offer 100+ quality control methods, including: - Struture Confirmation
- Purity
- Moisture
- Endotoxins
- Osmolarity
- Free Acid
- Sodium Ion Content
- Viscosity
- Etc
Additional QC option available based on modification type, stereochemistry, and development stage
Product List
Custom Services
siRNA miRNA ASO Aptamer sgRNA (up to 180nt)
Stock Products
Product Name Indication
- Givosiran (Givlaari) Acute Hepatic Porphyria
- Tofersern (Qalsody) Amyotrophic Lateral Sclerosis Type 1
- Eteplirsen (Exondys5l) Duchenne Muscular Dystrophy
- Viltolarsen (Viltepso) Duchenne Muscular Dystrophy
- Casimersen (Amondys54) Duchenne Muscular Dystrophy
- Volanesorsen (Waylivra) Familial Chylomicronemia Syndrome
- Fitusiran (Qfitlia) Hemophilia
- Inotersen ((Tegsed) Hereditary Transthyretin Amyloidosis
- Patisiran (Onpattro) Hereditary Transthyretin Amyloidosis
- Vutrisiran (Amvuttra) Hereditary Transthyretin Amyloidosis
- Inclisiran (Leqvio) Hypercholesterolemia
- Lumasiran (Oxlumo) Primary Hyperoxaluria Type 1
- Nedosiran ((Rivloza) Primary Hyperoxaluria Type 1
- Nusinersen (Spinraza) Spinal Muscle Atrophy
Rapid, high-purity, and professional therapeutics synthesis.
With 15 years of expertise in oligonucleotide synthesis, our supplier leverages a well-established oligonucleotide chemistry platform and a robust quality control system to deliver high-purity oligonucleotides ranging from nmol to hundred-gram scale. We provide integrated, one-stop support to accelerate the development of small nucleic acids therapeutics.
Product Features
Fast
- 2 mg – 5 mg
- 5 mg – 20 mg
- 20 mg -g-scale
High Purity: Purifity: > 90%
200+ Modifications
- GalNAc, lipid, peptide, a nd small molecule conjugation
- Antibody conjugation (ADC)
- Dual-target oligonucleotide
Stabilizing modifications: 2’Ome, 2’-O-OmE, 2’F, 2’-O-C16, LNA, cEt, GNA, UNA
Chemical Modification: Biotin, Dual Biotin, Amino linker C6, Amino linker C7, Amino linker C12, Cholesterol, Digoxigenin
Bases Modification: Pseudouridine, 1-Methyl-PseudoUridine, m6A, m5C, rl
Spacers & Linkers: dSpacer, PC-Linker, Spacer 9, Spacer, 18, Spacer C3, Spacer C6, Spacer C12, Inverted Abasic
Phosphorylation: Phosphate, Phosphorothioate, 5’-(E)-VP
Targeting Ligand Conjugation: GalNAc L96, NAG37, NAG25, 2’O-C16, avB6
Minimal Impurities
- Patented RNA synthesis technology
- Single impurity < 1%
Quality Control
We offer 100+ quality control methods, including: - Struture Confirmation
- Purity
- Moisture
- Endotoxins
- Osmolarity
- Free Acid
- Sodium Ion Content
- Viscosity
- Etc
Additional QC option available based on modification type, stereochemistry, and development stage
Product List
Custom Services
siRNA miRNA ASO Aptamer sgRNA (up to 180nt)
Stock Products
Product Name Indication
- Givosiran (Givlaari) Acute Hepatic Porphyria
- Tofersern (Qalsody) Amyotrophic Lateral Sclerosis Type 1
- Eteplirsen (Exondys5l) Duchenne Muscular Dystrophy
- Viltolarsen (Viltepso) Duchenne Muscular Dystrophy
- Casimersen (Amondys54) Duchenne Muscular Dystrophy
- Volanesorsen (Waylivra) Familial Chylomicronemia Syndrome
- Fitusiran (Qfitlia) Hemophilia
- Inotersen ((Tegsed) Hereditary Transthyretin Amyloidosis
- Patisiran (Onpattro) Hereditary Transthyretin Amyloidosis
- Vutrisiran (Amvuttra) Hereditary Transthyretin Amyloidosis
- Inclisiran (Leqvio) Hypercholesterolemia
- Lumasiran (Oxlumo) Primary Hyperoxaluria Type 1
- Nedosiran ((Rivloza) Primary Hyperoxaluria Type 1
- Nusinersen (Spinraza) Spinal Muscle Atrophy
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